Diseases curable by Cord
Blood Transplantation
Current &
Future applications of Cord Blood Transplantation
Since 1988, doctors have been
using cord blood in life saving treatments. Stem cell research
holds so much promise that the number of diseases and injuries
being treated is growing
rapidly.
Current Stem Cell
Applications:Leukemias , Lymphomas and other Blood
Cancers:
- Acute Biphenotypic
Leukemia†
- Acute Lymphocytic
Leukemia (ALL)
- Acute Myelogenous
Leukemia (AML)
- Acute Undifferentiated
Leukemia†
- Adult T Cell
Leukemia/Lymphoma
- Chronic Lymphocytic
Leukemia (CLL)
- Chronic Myelogenous
Leukemia (CML)
- Hodgkin's
Lymphoma
- Juvenile Chronic
Myelogenous Leukemia (JCML)
- Juvenile Myelomonocytic
Leukemia (JMML)
- Multiple
Myeloma
- Myeloid/Natural Killer
(NK) Cell Precursor Acute Leukemia
- Non-Hodgkin's
Lymphoma
- Prolymphocytic
Leukemia
- Plasma Cell
Leukemia
- Waldenstrom's
Macroglobulinemia
Other Cancers:
- Brain
Tumors††
- Ewing
Sarcoma†
- Neuroblastoma
- Ovarian
Cancer††
- Renal Cell
Carcinoma††
- Rhabdomyosarcoma
- Small-Cell Lung
Cancer††
- Testicular
Cancer††
- Thymoma (Thymic
Carcinoma)
Bone Marrow Failure
Disorders:
- Amegakaryocytosis
- Aplastic Anemia
(Severe)
- Blackfan-Diamond
Anemia
- Congenital
Cytopenia†
- Congenital
Dyserythropoietic Anemia
- Dyskeratosis
Congenita
- Fanconi
Anemia
- Paroxysmal Nocturnal
Hemoglobinuria (PNH)
- Pure Red Cell
Aplasia
Hemoglobinopaties:
- Beta Thalassemia
Major
- Sickle Cell
Disease
Histiocytic
Disorders:
- Failial
Erythrophagocytic Lymphohistiocytosis
- Hemophagocytosis
- Langerhans' Cell
Histiocytosis (Histiocytosis X)
Myelodysplastic/Myeloproliferative
Disorders:
- Acute
Myelofibrosis†
- Agnogenic Myeloid
Metaplasia (Myelofibrosis)†
- Amyloidosis • Chronic
Myelomonocytic Leukemia (CMML)
- Essential
Thrombocythemia† • Polycythemia Vera†
Refractory Anemias (RA)
including: Refractory Anemia with Excess Blasts (RAEB),
Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
& Refractory Anemia with Ringed Sideroblasts (RARS)
Inherited Metabolic Disorders:
- Adrenoleukodystrophy
- Fucosidosis
- Gaucher
Disease†
- Hunter Syndrome
(MPS-II)
- Hurler Syndrome
(MPS-IH)
- Krabbe
Disease
- Lesch-Nyhan
Syndrome
- Mannosidosis†
- Maroteaux-Lamy Syndrome
(MPS-VI)
- Metachromatic
Leukodystrophy
- Mucolipidosis II (I-cell
Disease)†
- Neuronal Ceroid
Lipofuscinosis (Batten Disease)†
- Niemann-Pick
Disease†
- Sandhoff
Disease†
- Sanfilippo Syndrome
(MPS-III)
- Scheie Syndrome
(MPS-IS)
- Sly Syndrome
(MPS-VII)
- Tay Sachs†
- Wolman
Disease
Inherited Immune System
Disorders:
- Chronic Granulomatous
Disease
- Congenital
Neutropenia
- Leukocyte Adhesion
Deficiency
- Severe Combined
Immunodeficiencies (SCID) including:
-
- Adenosine
Deaminase Deficiency†
- Bare Lymphocyte
Syndrome
- Chediak-Higashi
Syndrome†
- Kostmann
Syndrome
- Omenn
Syndrome
- Purine
Nucleoside Phosphorylase Deficiency
- Reticular
Dysgenesis
- Wiskott-Aldrich
Syndrome
- X-Linked
Lymphoproliferative Disorder Other Inherited
Disorders
- Cartilage-Hair
Hypoplasia
- Congenital
Erythropoietic Porphyria (Gunther Disease)
- DiGeorge
Syndrome
- Osteopetrosis
Other
- Chronic Active Epstein
Barr
- Evans
Syndrome
- Multiple
Sclerosis††
- Rheumatoid
Arthritis††
- Systemic Lupus
Erythematosus††
- Thymic Dysplasia
Emerging Stem Cell Applications††
- Brain Injury
- Cerebral
Palsy
- Type 1
Diabetes
- Heart
Disease
This list includes some
diseases that have been treated with bone marrow or peripheral
blood stem cells but have not yet been treated with cord blood
stem cells.
†Refer to clinical trials.gov for additional information.
††Not routinely eligible for CBR's Designated Transplant
Program® Source: Medical literature and clinical
trials
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